Disruption of a six-nucleotide miRNA motif improves PKD1 dosage and ameliorates polycystic kidney disease

Lakhia R, Song C, Biggers L, Zumwalt M, Alvarez J, Somasundaram A, Ramalingam H, Cobo-Stark P, Patel V. (2026). Disruption of a six-nucleotide miRNA motif improves PKD1 dosage and ameliorates polycystic kidney disease. Nucleic Acids Res. DOI: 10.1093/nar/gkaf1538 [Article] [DOI]