A novel gene therapy for ARPKD based on CFTR

Ciobanu C, Outeda P, Guggino WB, Cebotaru L. (2026). A novel gene therapy for ARPKD based on CFTR. Am J Physiol Gastrointest Liver Physiol. DOI: 10.1152/ajpgi.00109.2025. [Article] [DOI]