Collecting Duct-Targeted Lipid Nanoparticles Deliver Pkd2 mRNA to Restore Polycystin-2 and Attenuate ADPKD

Giblin J, Lambaren K, LaMastro R, Suzuki I, Huang Y, Simon R, Zarate-Diaz J, Osouli A, Pham J, Hallows K, Chung EJ. (2026). Collecting Duct-Targeted Lipid Nanoparticles Deliver Pkd2 mRNA to Restore Polycystin-2 and Attenuate ADPKD. bioRxiv. DOI: 10.64898/2026.06.02.728835 [Article] [DOI]